News

  1. Matt's story: I'm doing fine

    I’m lucky. It's been 4 years since the first MND symptoms, only my voice has been impacted.

    matt 2x

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  2. David's story: Nothing to lose

    Two and a half years after his diagnosis, David found a medicine with off-label application for MND.

    david 2x

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  3. New Parkinson's therapy approved by the FDA

    Kyowa Hakko Kirin's Parkinson's therapy, Nourianz (istradefylline), gains FDA approval as an add-on to levodopa/carbidopa.

    US flag thumbs up gesture

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  4. China approves edaravone for ALS

    Radicut/Radicava (edaravone), shown to slow the progression of ALS, is now approved for patients in China.

    China flag thumbs-uo hand gesture

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  5. SMC rejects two cystic fibrosis drugs

    Orkambi and Symkevi have been rejected by the Scotland Medicines Consortium (SMC) due to their conclusion that the costs outweigh the benefits.

    red haired girl on oxygen

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  6. EMA recommends approval of Vitrakvi (larotrectinib)

    Vitrakvi (larotrectinib) recommended by the CHMP for approval in the EU.

    EU approval OK hand gesture

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  7. Fiona's story: PBC, my mother and me

    fiona 2xAfter 40 years with primary biliary cholangitis, Fiona's mother is still alive thanks to her daughter's dedication and a liver transplant.

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  8. Marc's story: A brief look at life with ALS in the US

    After 3 years of living with ALS, Marc found a new medicine on the other side of the world. 

    marc 2x

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  9. Peter's story: Life goes on

    Diagnosed with ALS only 6 months ago, Peter went against the current to find more options to treat his disease.

    peter golfing close

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  10. Mark & Dee's story: For better, not worse

    With tears, laughter and hope, Mark and his family find their own way to cope with ALS.

    mark and dee 2x

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