News

I’m lucky. It's been 4 years since the first MND symptoms, only my voice has been impacted.

Two and a half years after his diagnosis, David found a medicine with off-label application for MND.

Kyowa Hakko Kirin's Parkinson's therapy, Nourianz (istradefylline), gains FDA approval as an add-on to levodopa/carbidopa.

Radicut/Radicava (edaravone), shown to slow the progression of ALS, is now approved for patients in China.

Orkambi and Symkevi have been rejected by the Scotland Medicines Consortium (SMC) due to their conclusion that the costs outweigh the benefits.

Vitrakvi (larotrectinib) recommended by the CHMP for approval in the EU.

After 40 years with primary biliary cholangitis, Fiona's mother is still alive thanks to her daughter's dedication and a liver transplant.

After 3 years of living with ALS, Marc found a new medicine on the other side of the world. 

Diagnosed with ALS only 6 months ago, Peter went against the current to find more options to treat his disease.

With tears, laughter and hope, Mark and his family find their own way to cope with ALS.