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Spinal Muscular Atrophy (SMA)


Available treatments for Spinal Muscular Atrophy (SMA)
You can order a treatment for Spinal Muscular Atrophy (SMA) via TheSocialMedwork if it has not been approved and/or is not available in the patient's country. TheSocialMedwork - helping patients and doctors access the latest approved medicines and at the lowest price possible worldwide.
Read more about Spinal Muscular Atrophy (SMA) below.
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Spinraza

(nusinersen)

by: Biogen Idec Ltd
for: Spinal Muscular Atrophy (SMA)
from: 96715.00
• EMA approved (EU)
• FDA approved (USA)
• PMDA approved (JAP)
• TGA approved (AUS)

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We may still be able to get it for you, provided that:

• it hasn't been approved and/or isn't available in your country
• you and your treating doctor have evaluated that the medicine is suitable for you, and your doctor writes a prescription for it.


About spinal muscular atrophy (sma)

Spinal muscular atrophy (SMA) is a hereditary disease that causes weakness and muscle wasting because of the loss of lower motor neurons controlling movement [1]. It results from a lack of survival motor neuron (SMN) protein, which is critical for the maintenance of motor neurons. Ultimately, individuals with the most severe type of SMA can become paralysed and have difficulty performing the basic functions of life, like breathing and swallowing [2].

SMA is estimated to occur in 1 in 6,000 to 1 in 10,000 live births [3]. Its severity correlates with the amount of SMN protein. People with Type 1 SMA, the most severe life-threatening form, produce very little SMN protein and don’t live beyond two years without respiratory support. People with Type 2 and Type 3 SMA produce greater amounts of SMN protein and have less severe, but still life-altering forms of SMA [2].

The above products may be suitable for treating patients with SMA. We recommend that you discuss the suitability of possible treatment options with your doctor. For further information please contact our support team at support@thesocialmedwork.com.



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