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Duchenne Muscular Dystrophy


Available treatments for Duchenne Muscular Dystrophy
You can order a treatment for Duchenne Muscular Dystrophy via TheSocialMedwork if it has not been approved and/or is not available in the patient's country. TheSocialMedwork - helping patients and doctors access the latest approved medicines and at the lowest price possible worldwide.
Read more about Duchenne Muscular Dystrophy below.
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Calcort

(deflazacort)

by: Sanofi
for: Several conditions involving inflammation in the body
from: 13.80
• MHRA approved (UK)
• BfArM approved (DE)

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We may still be able to get it for you, provided that:

• it hasn't been approved and/or isn't available in your country
• you and your treating doctor have evaluated that the medicine is suitable for you, and your doctor writes a prescription for it.


About duchenne muscular dystrophy

Duchenne muscular dystrophy (DMD) is a genetic neuromuscular disorder characterized by progressive muscle weakness and wasting [1]. It is caused by mutations in the dystrophin gene on the X-chromosome which result in an absence of the dystrophin protein [1], a protein that helps keep muscle cells intact [2].

It is the most prevalent neuromuscular disorder, affecting up to 1/3600 male births worldwide [1]. Symptoms onset is in early childhood, usually between ages 3 and 5. The disease primarily affects boys, but in rare cases, it can affect girls as well [2]. The standard therapy that can delay DMD progression is based on corticosteroids. The two mainly used in DMD are deflazacort and prednisone/prednisolone [1][3].

The above products may be suitable for treating patients with DMD. We recommend that you discuss the suitability of possible treatment options with your doctor. For further information please contact our support team at support@thesocialmedwork.com.


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